BRAINS FOR BRAIN Onlus Foundation (B4B)

ABOUT HLM RARE 2025

ABOUT HLM RARE 2025

Why this event matters

Drawing inspiration from the Draghi, Letta, and Heitor reports, the High-Level Meeting (HLM) will explore three central themes across the three days.

Day 1: Research & Innovation

Fostering competitive excellence in science and innovation through support for clinical trials and translational research.

Day 2: EU Infrastructure & Skills

Building pan-EU infrastructure to strengthen European Reference Networks and enhance capacity, including newborn screening and the use of data, registries and AI to expedite diagnosis and treatment initiation

Day 3: Policy & Funding

Overcoming fragmentation by establishing a coherent policy and funding regulatory framework specific to rare diseases, highlighting the importance of cross-border care

A central goal of the HLM Rare will be advocating for the EU’s adoption of a European Declaration on Rare and Complex Diseases, aiming to establish a sustainable Research and Innovation Ecosystem that ensures continuous dialogue and collaboration among all stakeholders.

Who should attend



Emoji Regulation

POLICY-MAKERS & REGULATORS



researchers

Clinicians & researchers



advocates

Patient & advocates



industry

Industry leaders

MEET THE ORGANISERS & STEERING COMMITTEE

The Organisers
Organisers

The steering committee

A number of European Reference Networks, supporting organisations and industry leaders listed below are part of the steering committee that is helping shape the event programme and the European Declaration on rare diseases.

Steering committee

OUR FUNDING & SPONSORS

We are grateful to the organisations and partners who make this event possible. Their support helps us bring together the global and European rare disease community to share knowledge, drive innovation and improve the lives of people living with rare diseases.

Funding providers